WWOX deficiency impairs neurogenesis and neuronal function in human organoids
Daniel J. Steinberg, Asia Zonca, Dania Abdellatif, Idan Rosh, I. M. Kustanovich, Osama Hidmi, Kian Maroun, Shani Stern, José Dávila-Velderrain, Rami I. Aqeilan
This study identifies WWOX mutations' impact on neurogenesis and neuronal function in human organoids, showing gene therapy can restore function.
bioRxiv · Dec 22, 2024 · PreprintNeuroscience