An all-in-one AAV vector for cardiac-specific gene silencing by an adenine base editor
Zhanzhao Liu, Luzi Yang, Yuhan Yang, Jiting Li, Zhan Chen, Congting Guo, Qianhao Guo, Qiuxuan Li, Yueshen Sun, Dongyu Zhao, Xiaomin Hu, Fei Gao, Yuxuan Guo
This study shows that single-AAV delivery of base editors can achieve effective cardiac gene silencing with higher success rates than dual-AAV systems.
bioRxiv · Sep 30, 2024 · PreprintMolecular Biology