Prime Editing Models the MTARC1 A165T Variant in Human Liver Organoids, Demonstrating Reduced Steatosis, Inflammation, and Fibrosis
Amel Ben Saad, Nahid Arghiani, Arden Weilheimer, Stefan D. Gentile, Benjamin J. Toles, Sudipta Tripathi, Seher Mohsin Sayed, Anil K. Chandraker, Alan C. Mullen
This study models the MTARC1 A165T variant in human liver organoids, showing reduced steatosis, inflammation, and fibrosis compared to reference sequence organoids.
Hepatology Communications · Sep 16, 2026Peer-reviewedCell Biology