CRISPR delivery particles for developing therapeutic strategies in metabolic disease
Y. Shen, J. L. Cohen, S. M. Nicoloro, M. Kelly, B. Yenilmez, F. Henriques, E. Tsagkaraki, Y. J. K. Edwards, X. Hu, R. H. Friedline, J. K. Kim, M. P. Czech
This study develops CRISPR delivery particles (CriPs) for efficient gene editing in cultured cells and in vivo, demonstrating their potential for therapeutic applications in metabolic disease.
bioRxiv · Jun 21, 2018Bioengineering