CRISPR-Cas9 Screens In Human Cells And Primary Neurons Identify Modifiers Of C9orf72 Dipeptide Repeat Protein Toxicity
Nicholas J. Kramer, Michael Seamus Haney, David W. Morgens, Ana Jovičić, Julien Couthouis, Amy Li, James A. Ousey, Rosanna K. Ma, Gregor Bieri, C. Kimberly Tsui, Yingxiao Shi, Nicholas T. Hertz, Marc Tessier‐Lavigne, Justin K. Ichida, Michael Cory Bassik, Aaron D. Gitler
Genome-wide CRISPR-Cas9 screens in human cells reveal mechanisms and targets for ALS-associated C9orf72 dipeptide repeat protein toxicity.
Nature Genetics · Feb 28, 2018Peer-reviewedGenetics