BiochemistryOphthalmology SciencePeer-reviewed
CTx001 for geographic atrophy: a gene therapy expressing soluble, truncated complement receptor 1 (mini-CR1)
Sonika Rathi, Athanasios Didangelos, Sofiya Pisarenka…·Simon J. Clark
This paper develops CTx001, a gene therapy expressing mini-CR1, which reduces MAC formation in a rat model of geographic atrophy.
3 citations