Reserpine maintains photoreceptor survival in retinal ciliopathy by resolving proteostasis imbalance and ciliogenesis defects
Holly Y. Chen, Manju Swaroop, Samantha Papal, Anupam Kumar Mondal, Hyun Beom Song, Laura Campello, Gregory J. Tawa, Florian Régent, Hiroko Shimada, Kunio Nagashima, Natalia de Val, Samuel G. Jacobson, Wei Zheng, Anand Swaroop
This study identifies reserpine as a drug candidate that improves photoreceptor survival in retinal ciliopathies by restoring proteostasis and ciliogenesis.
eLife · Mar 28, 2023Peer-reviewedGenetic & Genomic Medicine