NeurosciencebioRxivPreprint
A novel Ataxin-3 knock-in mouse model mimics the human SCA3 disease phenotype including neuropathological, behavioral, and transcriptional abnormalities
Eva Haas, Rana Dilara Incebacak Eltemur, Thomas Hentrich…·Jeannette Hübener‐Schmid
This paper describes a novel Ataxin-3 knock-in mouse model that replicates key neuropathological, behavioral, and transcriptional features of human SCA3 disease.
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