GDF5 modulation of MuSC pool as a potential therapeutic benefit for DMD
Christel Gentil, Aly Bourguiba, Amélie Vergnol, Bruno Cadot, Zoheir Guesmia, Lucile Saillard, Pierre Meunier, Bénédicte Hoareau‐Coudert, Mégane Lemaître, Sestina Falcone, Lorenzo Giordani, France Piétri‐Rouxel
This study shows that GDF5 overexpression in DMD mdx mice improves muscle histology, reduces inflammation, and enhances microdystrophin gene therapy outcomes.
Molecular Therapy — Nucleic Acids · Jul 7, 2026Peer-reviewedCell Biology