NeuroscienceNature CommunicationsPeer-reviewed
Mutant Huntingtin impairs neurodevelopment in human brain organoids through CHCHD2-mediated neurometabolic failure
Paweł Lisowski, Selene Lickfett, Agnieszka Rybak‐Wolf…·Alessandro Prigione
This study shows that mutant Huntingtin causes neurodevelopmental issues in human brain organoids by disrupting CHCHD2, leading to mitochondrial and metabolic problems.
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