Harnessing the power of whole human liver ex situ normothermic perfusion for preclinical AAV vector evaluation
Marti Cabanes‐Creus, Sophia H.Y. Liao, Renina Gale Navarro, Maddison Knight, Deborah Nazareth, Ngee‐Soon Lau, Mark Ly, Erhua Zhu, Ramon Roca-Pinilla, Ricardo Bugallo, Ana F. Vicente, Grober Baltazar, Adrian Westhaus, Jessica Merjane, Michael W. Crawford, , Leszek Lisowski
This study evaluates AAV vectors in human liver explants under normothermic perfusion to assess their functionality and neutralization by human sera.
Nature Communications · Mar 14, 2024Peer-reviewedMolecular Biology