NeuroscienceDisease Models & MechanismsPeer-reviewed
Human organoid model of PCH2a recapitulates brain region-specific pathology
Theresa Kagermeier, Stefan Hauser, Kseniia Sarieva…·Simone Mayer
This study develops human organoid models of PCH2a to investigate brain region-specific pathology, finding size reductions in cerebellar organoids and altered proliferation kinetics.
13 citationstop 3%