Prime editing for functional repair in patient-derived disease models
Imre Firmin Schene, Indi P. Joore, Rurika Oka, Michal Mokrý, Anke H.M. van Vugt, Ruben van Boxtel, Hubert P. J. van der Doef, Luc J. W. van der Laan, Monique M. A. Verstegen, Peter M. van Hasselt, Edward E. S. Nieuwenhuis, Sabine A. Fuchs
This paper demonstrates the use of prime editing to correct genetic mutations in patient-derived organoids, showing high efficiency and precision with minimal off-target effects.
Nature Communications · Oct 23, 2020Peer-reviewedGenomics