Efficient genome editing in the non-human primate brain using programmable extracellular vesicles
Xiuming Liang, Houze Zhou, Zubair Ahmed Nizamudeen, Eleni Kyriakopoulou, Angharad E. Evans, Samantha Roudi, Hernando Yesid Estupiñan, Julia Rädler, Vincent Hou, Callum D.W. Daniel, Inés Hernández-Pérez, Malika Singh, Pardis Parsi, Daniel A. Lonergan, Lidia Menéndez Berlana, , Samir EL Andaloussi
This paper demonstrates efficient genome editing in non-human primate brains using engineered extracellular vesicles, achieving therapeutic potential for neurological disorders.
bioRxiv · Aug 6, 2026 · PreprintMolecular Biology