Evaluation of Nav1.8 as a therapeutic target for Pitt Hopkins Syndrome
Keri Martinowich, Debamitra Das, Srinidhi Rao Sripathy, Yishan Mai, Rakaia F. Kenney, Brady J. Maher
The paper evaluates Nav1.8 as a therapeutic target for Pitt Hopkins Syndrome by reviewing literature and presenting data showing its inhibition normalizes neuron function and behavior in mouse models.
Molecular Psychiatry · Oct 12, 2022Peer-reviewedNeuroscience