Cell BiologybioRxivPreprint
Cardiac-Detargeted MyoAAV Enables Systemic Nrl-Mediated Fast Myofiber Remodeling and Hypertrophy Across Multiple Skeletal Muscles
Keisuke Hitachi, Shunya Sadaki, Masato Watanabe…·Ryo Fujita
This paper develops a modified MyoAAV vector that detargets cardiac expression, enabling safe systemic induction of fast myofiber remodeling and hypertrophy in skeletal muscles.
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