NeuroscienceEMBO Molecular MedicinePeer-reviewed
Fine-tuning FAM161A gene augmentation therapy to restore retinal function
Yvan Arsenijévic, Ning Chang, Olivier Mercey…·Corinne Kostic
This study fine-tunes FAM161A gene therapy in mice to restore retinal function by optimizing promoter activity, dosage, and isoform delivery.
14 citations