Daniel J. Ham

This paper describes a dual AAV gene therapy approach using linker proteins to restore basement membrane function in LAMA2 MD, showing significant improvements in muscle and nerve defects.

This study shows that muscle fiber Myc is not required for muscle growth but its overexpression disrupts muscle structure and function.

This study shows that mTORC1 inhibition in adult mice does not cause muscle atrophy or functional decline, despite metabolic and morphological changes.