Molecular BiologybioRxivPreprint
Efficient Cas9 nuclease-based editing in skeletal muscle via lipid nanoparticle delivery
Sukanya Iyer, Katelyn Daman, Yehui Sun…·Scot A. Wolfe
SORT LNPs enable efficient Cas9-mediated repair of a pathogenic allele in skeletal muscle in a mouse model of LGMDR7.
3 citations