A novel imaging ligand as a biomarker for mutant huntingtin-lowering in Huntington's disease
Daniele Bertoglio, Jonathan Bard, Manuela Heßmann, Longbin Liu, Annette Gärtner, Stef De Lombaerde, Britta Huscher, Franziska Zajicek, Alan Miranda, Finn Peters, Frank Herrmann, Sabine Schaertl, Tamara Vasilkovska, Christopher J Brown, Peter D Johnson, , Ignacio Muñoz-Sanjuán
This paper develops a PET radioligand to visualize mutant huntingtin levels in the brain and assess therapeutic interventions in Huntington's disease.
bioRxiv · Jul 9, 2021 · PreprintNeuroscience