Nitazoxanide activates BMP9-ALK1-SMAD signaling cascade and improves HHT vascular pathology
Camila Chiesa, Valentina Pérez-Torrado, Letizia Nada, Rossana Mezzano, Carolina Vázquez, Leonardo Santos, Zelika Criscuolo, Marcelo Serra, Philippe Marambaud, Carlos Escande, Santiago Ruiz
This study shows nitazoxanide activates BMP9-ALK1-SMAD signaling and reduces HHT vascular abnormalities by modulating mTOR activity in endothelial cells.
bioRxiv · May 14, 2026 · PreprintCell Biology