Anti-seizure Gene Therapy for Focal Cortical Dysplasia
Amanda Almacellas‐Barbanoj, R. Graham, Benito Maffei, Jenna C. Carpenter, Marco Leite, Justin Hoke, Felisia Hardjo, James Scott-Solache, Christos Chimonides, Stéphanie Schorge, Dimitri Michael Kullmann, Vincent Magloire, Gabriele Lignani
This paper evaluates gene therapy using Kv1.1 potassium channel overexpression in a mouse model of FCD, showing reduced seizures but no improvement in cognitive or behavioral issues.
Brain · Nov 20, 2023Peer-reviewedNeuroscience