A truncated reverse transcriptase enhances prime editing by split AAV vectors
Zongliang Gao, Sujan Ravendran, Nanna S. Mikkelsen, Jakob Haldrup, Huiqiang Cai, Xiangning Ding, Søren R. Paludan, Martin Kristian Thomsen, Jacob Giehm Mikkelsen, Rasmus Otkjær Bak
This paper improves prime editing by modifying the reverse transcriptase component to enhance efficiency and enable delivery via split AAV vectors.
Molecular Therapy · Jul 8, 2022Peer-reviewedGenetics