NeurosciencebioRxivPreprint
Early pathogenesis of spinal and bulbar muscular atrophy uncovered by human iPSC-derived motor neurons highlights pathogenic neuropeptides as therapeutic targets
Kazunari Onodera, Yuichi Riku, Daisuke Shimojo…·Yohei Okada
The paper uses human iPSC-derived motor neurons to study SBMA, identifying neuropeptides as therapeutic targets.
DOI 10.64898/2025.12.10.692869