A Singular Base Editing Platform for Polyfunctional Multiplex Engineering of Immune Cells
Joseph G. Skeate, Nicholas J. Slipek, Walker S. Lahr, Shambojit Roy, Bryce J. Wick, Bibekananda Kar, Jae-Woong Chang, Erin M. Stelljes, Alexandria K. Gilkey, Prateek P. Thenge, Miechaleen D. Diers, Joshua B. Krueger, Ethan M. Niemeyer, Cara-lin Lonetree, Mitchell G. Kluesner, , Beau R. Webber
This paper develops a base editing platform to efficiently and safely engineer CAR T cells with multiple gene knockouts and insertions.
Molecular Therapy · Jul 18, 2026Peer-reviewedBioengineering