GeneticsbioRxivPreprint
Cardiac Applications of CRISPR/AAV-Mediated Precise Genome Editing
Yanjiang Zheng, Joshua Mayourian, Justin S. King…·Nathan J. VanDusen
This study applies CASAAV-HDR to model cardiomyopathies and perform functional genomics in mouse cardiomyocytes, showing its utility for disease modeling and enhancer analysis.
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